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Muscle Gene Therapy CONGENITAL MYATHENIC SYNDROME Quantitative microdialysis DMPK Knockout Maximal force Myotonic dystrophy mouse models BIOLOGIE MOLECULAIRE AAV Dystrophin CMS Animals KNOCKOUT MICE Exercise Long read sequencing Brain dysfunction Mice Genotype phenotype correlation Myotonic dystrophy Therapy Oligodendrocyte Trinucleotide Repeat Expansion Desmin Myelin Dystrophie Myotonique Diaphragm Myotonic Dystrophy Type 1 Myotonic dystrophy type 1 Oligodendrocytes CTG repeat contractions Glial cells Transcriptomics DM1 CTG repeat instability ARN Fibrosis Acute coronary syndrome Mouse model Acetylcholinesterase deficiency In vivo Acetylcholinesterase knockout mouse Antisense oligonucleotides Cardiac muscle Transgenic mouse model CRISPRi Dynamin 2 Dystrophie myotonique Brain Astrocytes Trinucleotide repeat expansion RNA interference Heart failure Duchenne muscular dystrophy Hypoxia Gene editing GABA PCR Humans Alternative splicing Cell model MBNL Centronuclear myopathy Cytoskeleton Muscular dystrophy Aging CTG repeats Glucocorticoid-receptor Autophagy Central nervous system Male Myotonic Dystrophy type 1 Motoneuron PacBio Expression Exercice RNA splicing Astrocyte Gene therapy Dilated cardiomyopathy Skeletal muscle Thérapie génique GSK3␤ ACETYLCHOLINESTERASE Mouse models Transgenic mouse Lc3 Glucocorticoids Intermediate filament RNA biology Antisense oligonucleotide Cell penetrating peptide Heart Myotonic Dystrophy Glutamate Cell culture model DMSXL mice Neuron CRISPR/Cas9 Myostatin