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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Multi exon skipping
Cell Biology
Dynamin 2
Metabolism
Calcium Channels
Autophagy
Modificateurs de gènes
Exon skipping
Knockout
Génomique
Dystrophie Musculaire de Becker BMD
Long QT
Myogenesis
Dystrophine
NAD+
LKB1
Animal/physiopathology
Muscular Atrophy
L-Type
Dystrophin
Mdx mouse
Energy Metabolism/drug effects
Morphogenesis
CD38
Clinical trials
Dystrophy
Allele‐specific silencing therapy
Animals
MES
Male
Cell homeostasis
Multi resolution modeling
Long noncoding RNA
Dystrophie musculaire de Becker
Drp1
Becker muscular dystrophy BMD
BMD
Molecular Sequence Data
Skeletal muscle
Muscular Dystrophy
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Mice
Cell Line
Dystrophin-EGFP
Dystrophie Musculaire de Duchenne DMD
Muscles/physiopathology
Cachexia
Becker BMD muscular dystrophy
DMO
Muscle
Muscle development
Cells
Liver
Genomic
CaVβs
Invivo
CTNNB1
Inbred mdx
Muscle Biology
Gene expression
Becker muscular dystrophy
CaV subunits
Hepatocellular carcinoma
Duchenne muscular dystrophy DMD
Base Sequence
Diseases
Duchenne muscular dystrophy
Gene modifiers
MiARN
Inbred C57BL
Activin Receptors
Ex-vivo
Multiresolution modeling
DHPR α1S
Homeostasis
LncRNA
Hear
Human Umbilical Vein Endothelial Cells
Inhibitors
Humans
Delivery
Mitochondrial fission
LncARN
Gene Expression Regulation/drug effects
Muscle Strength
Cardiomyopathy
Cardiomyopathie
Cultured
Epigenetics
Antisense oligonucleotides
Myotendinous junction
Calcium
DMD
Duchenne DMD dystrophy
Molecular docking
Dystrophin central domain
NNOS
Centronuclear myopathy
Immunoglobulin Fc Fragments/pharmacology
Muscular dystrophy