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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
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Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Cells
Becker BMD muscular dystrophy
Epigenetics
Dystrophie Musculaire de Becker BMD
Dystrophie musculaire de Becker
Dystrophie Musculaire de Duchenne DMD
NAD+
Cell Line
LncARN
Dynamin 2
LKB1
Myotendinous junction
Muscle
Inhibitors
Inbred C57BL
Liver
Becker muscular dystrophy
Multi resolution modeling
Dystrophy
Muscular Dystrophy
Energy Metabolism/drug effects
Cultured
Knockout
Modificateurs de gènes
Calcium
Exon skipping
Drp1
Mitochondrial fission
Centronuclear myopathy
Autophagy
DMO
Metabolism
Molecular docking
Duchenne muscular dystrophy
Hear
Génomique
Muscle Strength
Gene modifiers
DMD
CTNNB1
Multiresolution modeling
L-Type
Diseases
Molecular Sequence Data
Muscles/physiopathology
Clinical trials
Human Umbilical Vein Endothelial Cells
Gene expression
Allele‐specific silencing therapy
MiARN
Antisense oligonucleotides
Dystrophin
Base Sequence
CaVβs
MES
Muscular Atrophy
Inbred mdx
Long QT
Muscular dystrophy
Dystrophine
NNOS
CaV subunits
Animal/physiopathology
Skeletal muscle
Cell homeostasis
Long noncoding RNA
Mice
Activin Receptors
Animals
Genomic
Myogenesis
Duchenne DMD dystrophy
Ex-vivo
Cell Biology
Humans
Delivery
Dystrophin central domain
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Calcium Channels
Male
Becker muscular dystrophy BMD
Muscle Biology
DHPR α1S
Immunoglobulin Fc Fragments/pharmacology
Invivo
Homeostasis
Cardiomyopathie
Cachexia
Mdx mouse
Gene Expression Regulation/drug effects
Hepatocellular carcinoma
Muscle development
Morphogenesis
LncRNA
Dystrophin-EGFP
Duchenne muscular dystrophy DMD
Cardiomyopathy
Multi exon skipping
CD38
BMD